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Patient Daily
| Dec 11, 2025
FDA halts Denali's Pompe therapy over preclinical safety signals
Patient Daily
| Dec 11, 2025
Praxis halts epilepsy trial early after positive results; prepares for FDA discussions
Patient Daily
| Dec 11, 2025
CDC advisory panel recommends delaying hepatitis B vaccine dose for some newborns
Patient Daily
| Dec 11, 2025
FDA plans to lower clinical trial requirements for new drug approvals
Patient Daily
| Dec 11, 2025
Crescent Biopharma and Kelun-Biotech sign cancer therapy deal worth up to $1.25 billion
Patient Daily
| Dec 11, 2025
FDA issues draft guidance reducing animal testing requirements for some products
Patient Daily
| Dec 11, 2025
FDA considers raising user fees for foreign-based phase I clinical trials
Patient Daily
| Dec 11, 2025
FDA confirms tougher review process ahead for uniQure's Huntington's gene therapy
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Pharmaceuticals
Patient Daily
| Jan 27, 2026
Rare disease drug developers outline strategies at J.P. Morgan Healthcare conference
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Pharmaceuticals
Patient Daily
| Jan 27, 2026
FDA extends review timelines for four priority voucher drugs
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Pharmaceuticals
Patient Daily
| Jan 30, 2026
Senate gridlock delays decision on rare disease priority review voucher program
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Pharmaceuticals
Patient Daily
| Jan 27, 2026
SpyGlass Pharma and AgomAb Therapeutics file for Nasdaq IPOs
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