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National Organization for Rare Disorders (Nord)
Marian Johns | Jan 18, 2018

National Organization For Rare Disorders encouraging participation in 7,000 mile effort to raise awareness
Marian Johns | Nov 16, 2017

Patient groups say Orphan Drug Tax Credit repeal could result in fewer treatments for rare diseases
Russell Boniface | Sep 13, 2017

FDA approves first gene therapy for leukemia
Keri Carbaugh | Dec 28, 2016

Rare disease forces family to leave state for better care
Jeff Gantt | Dec 16, 2016

NORD RAN releases second state report on rare diseases
Keri Carbaugh | Dec 9, 2016

House representatives pass National Defense Authorization Act
Amanda Rupp | Nov 12, 2016

Novel study launches for FD/MAS
Amanda Rupp | Oct 5, 2016

Keynote speakers announced for 2016 Rare Diseases and Orphan Products Breakthrough Summit

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+ Pharmaceuticals
Patient Daily | Jun 18, 2025

ENT specialist on acid reflux: ‘You actually have a structural issue that may predispose you to sinusitis’
+ Pharmaceuticals
Patient Daily | Jun 16, 2025

American Consumer Institute questions hospital use of 340B Drug Pricing Program
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Patient Daily | Jun 13, 2025

Data scientist: ‘340B sales growth was 115.5% higher than the growth of non-340B sales in 2023’
+ Pharmaceuticals
Patient Daily | Jun 19, 2025

Patients Come First spokesperson on 340B reform: ‘Americans deserve a system that prioritizes patients first, not pharmacy middlemen’