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National Organization for Rare Disorders (Nord)
Marian Johns | Jan 18, 2018

National Organization For Rare Disorders encouraging participation in 7,000 mile effort to raise awareness
Marian Johns | Nov 16, 2017

Patient groups say Orphan Drug Tax Credit repeal could result in fewer treatments for rare diseases
Russell Boniface | Sep 13, 2017

FDA approves first gene therapy for leukemia
Keri Carbaugh | Dec 28, 2016

Rare disease forces family to leave state for better care
Jeff Gantt | Dec 16, 2016

NORD RAN releases second state report on rare diseases
Keri Carbaugh | Dec 9, 2016

House representatives pass National Defense Authorization Act
Amanda Rupp | Nov 12, 2016

Novel study launches for FD/MAS
Amanda Rupp | Oct 5, 2016

Keynote speakers announced for 2016 Rare Diseases and Orphan Products Breakthrough Summit

Trending
Patient Daily | Aug 12, 2025

Capitol Breathe Free Otolaryngologist on air quality and pollution: ‘These are common triggers for sinus inflammation and sinus infections’
+ Regulatory
Patient Daily | Aug 14, 2025

Founder of Policy Candy: '340B must see comprehensive reforms'
+ Pharmaceuticals
Patient Daily | Aug 18, 2025

Patients Come First spokesperson on 340B rebate model: ‘This rebate model provides the oversight that 340B has needed for decades’
+ Pharmaceuticals
Patient Daily | Aug 14, 2025

PhRMA COO on 340B: 'Hidden tax on patients, taxpayers & employers'