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Patient Daily
| Mar 4, 2026
FDA proposes regulatory path for individualized gene editing therapies targeting rare diseases
Patient Daily
| Mar 4, 2026
Congress approves record $315 million for ALS research amid new treatment efforts
Patient Daily
| Mar 4, 2026
Appellate court rules for REGENXBIO over Sarepta in gene therapy patent case
Patient Daily
| Mar 4, 2026
Novo Nordisk’s obesity drug fails key test against Eli Lilly rival
Patient Daily
| Mar 4, 2026
Gilead announces plan to acquire Arcellx for $7.8 billion ahead of FDA decision
Patient Daily
| Mar 4, 2026
Gene therapies for sickle cell disease face slow uptake despite early promise
Patient Daily
| Mar 4, 2026
Study finds bilingualism does not disrupt parent-child brain synchrony during play
Patient Daily
| Mar 4, 2026
Study shows high rate of off-label antipsychotic use among Finnish seniors
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Pharmaceuticals
Patient Daily
| Mar 22, 2026
BioMarin pauses dosing and enrollment in two Voxzogo studies after safety signal
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Regulatory
Patient Daily
| Mar 20, 2026
Neurosurgeon DiGiorgio on 340B: '340B also takes money from taxpayers and makes everyone’s health insurance more expensive'
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Pharmaceuticals
Patient Daily
| Mar 22, 2026
FDA rejects REGENXBIO’s Hunter syndrome therapy as Denali awaits decision on rival drug
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Pharmaceuticals
Patient Daily
| Mar 25, 2026
Revolution and Ascendis identified as top buyout targets amid speculation of industry mega-merger
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